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Emerging Genetic Treatments for SCN8A and a look at n-of-1/nLorem
September 24, 2022 @ 10:30 am - 11:30 am EDT
Join us to hear from SCN8A parents and researchers, Madeleine Oudin and Chris Burge, to learn about different kinds of emerging genetic therapies, what is in the pipeline for SCN8A and hear about their journey to find an ASO treatment for their daughter, Margot, with a new company called nLorem.
You can register in advance HERE.
*This image of an ASO treatment was taken from our SCN8A Unraveled discussion with Sophie Hill, who is working in the lab of Miriam Meisler, on an ASO treatment for SCN8A. You can read that interview here or watch the episode here.
We would like to extend our thanks to Neurocrine Biosciences and Praxis Precision Medicines for their support of these meetings which bring improved quality of life to families and allows them opportunities to learn, connect, and contribute to the understanding of SCN8A.