International SCN8A Alliance Logo

Emerging Genetic Treatments for SCN8A and a look at n-of-1/nLorem

Join us to hear from SCN8A parents and researchers, Madeleine Oudin and Chris Burge, to learn about different kinds of emerging genetic therapies, what is in the pipeline for SCN8A and hear about their journey to find an ASO treatment for their daughter, Margot, with a new company called nLorem. You can register in advance […]

We would like to extend our thanks to Neurocrine Biosciences and Praxis Precision Medicines for their support of these meetings which bring improved quality of life to families and allows them opportunities to learn, connect, and contribute to the understanding of SCN8A.